Crispr gene-editing ‘revolution’ treats internal organ for first time Crispr基因编辑“革命”首次被用于治疗内脏
US start-up co-founded by Nobel laureate marks breakthrough over therapies restricted to external cells 美国初创企业Intellia的早期试验数据标志着Crispr疗法取得突破,表明科学家克服了此前仅能将该技术用于编辑体外细胞的局限。